The agency also revoked Sarepta's platform technology designation for AAVrh74 Friday and issued a safety communication saying ...

As mothers of children with this disease, we have wept helplessly in recent months as friends — fellow members of a club we ...

Sarepta stock tanked Friday after a new patient death was uncovered, spurring an FDA request to halt shipments of an ...

U.S. stocks are rising toward more records on Monday ahead of a week full of profit updates from big U.S. companies.

A standoff over Elevidys could have major consequences for Duchenne patients, gene therapy companies and the perception of ...