RAPS

EMA Announces Sweeping Overhaul of Pediatric Class Waivers

In a major move, the European Medicines Agency (EMA) announced today it is revoking or revising most product class waivers that allow companies to bypass the requirement to test new drugs in pediatric ...
Tennessean

Brim Analytics to Participate in ARPA-H Pediatric Cancer eXpansion to Help Scale Best-in-Class Care Nationwide

NASHVILLE, TN, UNITED STATES, January 14, 2026 /EINPresswire.com/ — Brim Analytics today announced its participation in the Advanced Research Projects Agency for ...
Yahoo Finance

Circle Pharma Announces Poster Presentation Highlighting the Potential of CID-078, a First-in-class Oral Cyclin A/B RxL Inhibitor, at the American Association for Cancer ...

SAN FRANCISCO, September 25, 2025--(BUSINESS WIRE)--Circle Pharma, Inc., a clinical-stage biopharmaceutical company pioneering next-generation targeted macrocycle therapeutics for cancer, today ...
Business Wire

AVROBIO Receives Rare Pediatric Disease Designation from the U.S. FDA for First-in-Class Gene Therapy for Gaucher Disease

Our first-in-class pipeline includes clinical programs for cystinosis and Gaucher disease type 1, as well as preclinical programs for Gaucher disease type 3, Hunter syndrome and Pompe disease. Our ...
Nasdaq

Day One Expands Pipeline with Potential First-in-Class Clinical-Stage Antibody Drug Conjugate (ADC) Targeting PTK7 in Solid Tumors for Adult and Pediatric Cancers

BRISBANE, Calif., June 18, 2024 (GLOBE NEWSWIRE) -- Day One Biopharmaceuticals (Nasdaq: DAWN) (“Day One” or the “Company”), a commercial-stage biopharmaceutical company dedicated to developing and ...
The Florida Times-Union

Brim Analytics to Participate in ARPA-H Pediatric Cancer eXpansion to Help Scale Best-in-Class Care Nationwide

Participation supports national effort to unlock cures for pediatric cancer using artificial intelligence. NASHVILLE, TN, UNITED STATES, January 14, 2026 ...