NJ.com

What is muscular dystrophy, the rare genetic disease Gilbert Gottfried had?

Tributes flooded the internet for Gilbert Gottfried after his family shared on Tuesday via Twitter that he died following “a long illness.” Since then, there has been more awareness around muscular ...
kristv

Local mother advocates for muscular dystrophy disease with 'Fill the Boot' Campaign

is your neighborhood reporter for North Beach, Downtown Corpus Christi and the Bay Area. CORPUS CHRISTI, Texas — A local mother is raising awareness for Duchenne muscular dystrophy (DMD) as her son ...
MedCity News

FDA Nod in Duchenne Helps Wider Swath of Patients With the Rare Muscle Disease

Duchenne muscular dystrophy has several approved drugs, including a gene therapy that provides children who have the rare, inherited muscle-wasting disease the option of a one-time treatment. But each ...
Everyday Health

Speaking Muscular Dystrophy: A Glossary of Terms Used to Describe Symptoms, Tests, Treatments, and More

This quick alphabetical guide will help you feel more confident when talking about muscular dystrophy with your doctor and loved ones. Muscular dystrophy is the name for a group of genetic diseases ...
The American Journal of Managed Care

Quantifying the Altruism Value for a Rare Pediatric Disease: Duchenne Muscular Dystrophy

Altruism values for treatments of rare, severe pediatric diseases have not been estimated. This study found the altruism value for a hypothetical new Duchenne muscular dystrophy treatment to be $80 ...

Nxera Pharma Licenses Japan and Select Asia-Pacific Rights to Vamorolone for Duchenne Muscular Dystrophy from Santhera Pharmaceuticals

Vamorolone is approved and marketed as AGAMREE® for the treatment of Duchenne Muscular Dystrophy (DMD) in the US, European Union, UK and ChinaNew ...
Medical Xpress

Disease or Syndrome: Muscular Dystrophy, Duchenne

If cancer is a disease of overabundance, where cells divide without restraint and tumors grow despite the body's best interests, then degenerative diseases are disorders of deprivation. When ...
The Beaumont Enterprise on MSN

How SETX WhiskeyFest helps the Cure Rare Disease nonprofit

Southeast Texas WhiskeyFest proceeds will support the Cure Rare Disease nonprofit, which has become a life mission for Mike ...
Business Wire

Promising disease modifying approach to Duchenne muscular dystrophy with Neu-REFIX® Beta 1,3-1,6 glucan* from Japan; the first such clinical report.

TOKYO--(BUSINESS WIRE)--Duchenne Muscular Dystrophy (DMD) patients showed signs of disease progress slowing down, after oral consumption of Neu REFIX ß-glucan for 45 days along with routine ...
Yahoo Finance

Muscular Dystrophy Association Announces More Than $2.7 Million For Research Grants to Advance Breakthroughs Across Neuromuscular Diseases

New York, Dec. 10, 2025 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) today announced more than $2.7 million in new research grants to advance groundbreaking discoveries across multiple ...
Medical News Today

What is congenital muscular dystrophy?

Congenital muscular dystrophy (CMD) is a disease that affects certain muscles. Individuals with CMD may experience symptoms such as muscle weakness and joint problems. “Congenital” means present since ...